The path to successful commercialization of cell and gene therapies: empowering patient advocates

Gerhard Bauer, Mohamed Abou-El-Enein, Alastair Kent, Brian Poole, Miguel Forte

Research output: Contribution to journalArticle

4 Scopus citations

Abstract

Often, novel gene and cell therapies provide hope for many people living with incurable diseases. To facilitate and accelerate a successful regulatory approval and commercialization path for effective, safe and affordable cell and gene therapies, the involvement of patient advocacy groups (PAGs) should be considered early in the development process. This report provides a thorough overview of the various roles PAGs play in the clinical translation of cell and gene therapies and how they can bring about positive changes in the regulatory process, infrastructure improvements and market stability.

Original languageEnglish (US)
Pages (from-to)293-298
Number of pages6
JournalCytotherapy
Volume19
Issue number2
DOIs
StatePublished - Feb 1 2017

Keywords

  • affordability
  • cell and gene therapies
  • clinical trials commercialization
  • patient advocacy
  • regulation
  • reimbursement

ASJC Scopus subject areas

  • Immunology and Allergy
  • Immunology
  • Oncology
  • Genetics(clinical)
  • Cell Biology
  • Cancer Research
  • Transplantation

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