Long-term, high-level hepatic secretion of acid α-glucosidase for Pompe disease achieved in non-human primates using helper-dependent adenovirus

D. P.W. Rastall, S. S. Seregin, Y. A. Aldhamen, L. M. Kaiser, C. Mullins, A. Liou, Frank Ing, C. Pereria-Hicks, S. Godbehere-Roosa, D. Palmer, P. Ng, A. Amalfitano

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