Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning

Manuela Corti, Brian Cleaver, Nathalie Clément, Thomas J. Conlon, Kaitlyn J. Faris, Gensheng Wang, Janet Benson, Alice F Tarantal, Davis Fuller, Roland W. Herzog, Barry J. Byrne

Research output: Contribution to journalArticle

33 Scopus citations

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