• 8589 Citations
  • 48 h-Index
1986 …2020

Research output per year

If you made any changes in Pure these will be visible here soon.

Research Output

Filter
Review article
2018

A checklist for clinical trials in rare disease: Obstacles and anticipatory actions-lessons learned from the FOR-DMD trial

Crow, R. A., Hart, K. A., McDermott, M. P., Tawil, R., Martens, W. B., Herr, B. E., McColl, E., Wilkinson, J., Kirschner, J., King, W. M., Eagle, M., Brown, M. W., Hirtz, D., Lochmuller, H., Straub, V., Ciafaloni, E., Shieh, P. B., Spinty, S., Childs, A. M., Manzur, A. Y. & 28 others, Morandi, L., Butterfield, R. J., Horrocks, I., Roper, H., Flanigan, K. M., Kuntz, N. L., Mah, J. K., Morrison, L., Darras, B. T., von der Hagen, M., Schara, U., Wilichowski, E., Mongini, T., McDonald, C. M., Vita, G., Barohn, R. J., Finkel, R. S., Wicklund, M., McMillan, H. J., Hughes, I., Pegoraro, E., Bryan Burnette, W., Howard, J. F., Thangarajh, M., Campbell, C., Griggs, R. C., Bushby, K. & Guglieri, M., May 10 2018, In : Trials. 19, 1, 291.

Research output: Contribution to journalReview article

5 Scopus citations
2017

Advances in pulmonary care in duchenne muscular dystrophy

Mayer, O. H., Henricson, E. K., McDonald, C. M. & Buyse, G. M., 2017, In : European Neurological Review. 13, 1, p. 35-41 7 p.

Research output: Contribution to journalReview article

7 Scopus citations

Pulmonary Endpoints in Duchenne Muscular Dystrophy. A Workshop Summary

Finder, J., Mayer, O. H., Sheehan, D., Sawnani, H., Abresch, R. T., Benditt, J., Birnkrant, D. J., Duong, T., Henricson, E. K., Kinnett, K., McDonald, C. M. & Connolly, A. M., Aug 15 2017, In : American Journal of Respiratory and Critical Care Medicine. 196, 4, p. 512-519 8 p.

Research output: Contribution to journalReview article

23 Scopus citations
2005

Practice Parameter: Corticosteroid treatment of Duchenne dystrophy - Report of the Quality Standards Subcommittee of the American Academy of Neurology and the Practice Committee of the Child Neurology Society

Moxley, R. T., Ashwal, S., Pandya, S., Connolly, A., Florence, J., Mathews, K., Baumbach, L., McDonald, C. M., Sussman, M. & Wade, C., Jan 11 2005, In : Neurology. 64, 1, p. 13-20 8 p.

Research output: Contribution to journalReview article

243 Scopus citations